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In vivo base editing of a pathogenic Eif2b5 variant improves vanishing white matter phenotypes in mice
Böck, D., Revers, I. M., Bomhof, A. S. J., Hillen, A. E. J., Boeijink, C., Kissling, L., Egli, S., Moreno-Mateos, M. A., van der Knaap, M. S., van Til, N. P. & Schwank, G., 1 May 2024, In: Molecular therapy. 32, 5, p. 1328-1343 16 p.Research output: Contribution to journal › Article › Academic › peer-review