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Development of medicines for rare diseases and inborn errors of metabolism: Toward novel public–private partnerships
Rosenberg, N., Stolwijk, N. N., van den Berg, S., Heus, J. J., van der Wel, V., van Gelder, T., Bosch, A. M., de Visser, S. J. & Hollak, C. E. M., Sept 2023, In: Journal of inherited metabolic disease. 46, 5, p. 806-816 11 p.Research output: Contribution to journal › Review article › Academic › peer-review
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Access to medicines for rare diseases: A European regulatory roadmap for academia
Rosenberg, N., van den Berg, S., Stolwijk, N. N., Jacobs, B. A. W., Post, H. C., Pasmooij, A. M. G., de Visser, S. J. & Hollak, C. E. M., 2023, In: Frontiers in pharmacology. 14, 1142351.Research output: Contribution to journal › Article › Academic › peer-review
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Clinical impact of the worldwide shortage of verteporfin (Visudyne®) on ophthalmic care
Sirks, M. J., van Dijk, E. H. C., Rosenberg, N., Hollak, C. E. M., Aslanis, S., Cheung, C. M. G., Chowers, I., Eandi, C. M., Freund, K. B., Holz, F. G., Kaiser, P. K., Lotery, A. J., Ohno-Matsui, K., Querques, G., Subhi, Y., Tadayoni, R., Wykoff, C. C., Zur, D., Diederen, R. M. H., Boon, C. J. F., & 1 others, 1 Nov 2022, In: Acta ophthalmologica. 100, 7, p. e1522-e1532Research output: Contribution to journal › Article › Academic › peer-review
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