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Gene Therapy in Patients with the Crigler-Najjar Syndrome
D'Antiga, L., Beuers, U., Ronzitti, G., Brunetti-Pierri, N., Baumann, U., di Giorgio, A., Aronson, S., Hubert, A., Romano, R., Junge, N., Bosma, P., Bortolussi, G., Muro, A. F., Soumoudronga, R. F., Veron, P., Collaud, F., Knuchel-Legendre, N., Labrune, P. & Mingozzi, F., 17 Aug 2023, In: The New England journal of medicine. 389, 7, p. 620-631 12 p.Research output: Contribution to journal › Article › Academic › peer-review
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What’s next in gene therapy for Crigler-Najjar syndrome?
Aronson, S. J., Ronzitti, G. & Bosma, P. J., 2023, In: Expert Opinion on Biological Therapy. 23, 2, p. 119-121 3 p.Research output: Contribution to journal › Editorial › Academic › peer-review
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Disease burden and management of Crigler-Najjar syndrome: Report of a world registry
CureCN Consortium, 1 Jul 2022, In: Liver international. 42, 7, p. 1593-1604 12 p.Research output: Contribution to journal › Article › Academic › peer-review
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