Amsterdam Gastroenterology Endocrinology Metabolism
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Repurposing empagliflozin in individuals with glycogen storage disease Ib: A value-based healthcare approach and systematic benefit-risk assessment
Derks, T. G. J., Venema, A., Köller, C., Bos, E., Overduin, R. J., Stolwijk, N. N., Hofbauer, P., Bolhuis, M. S., van Eenennaam, F., Groen, H., Hollak, C. E. M. & Wortmann, S. B., Mar 2024, In: Journal of inherited metabolic disease. 47, 2, p. 244-254 11 p.Research output: Contribution to journal › Article › Academic › peer-review
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Food or medicine? A European regulatory perspective on nutritional therapy products to treat inborn errors of metabolism
Stolwijk, N. N., Bosch, A. M., Bouwhuis, N., Häberle, J., van Karnebeek, C., van Spronsen, F. J., Langeveld, M. & Hollak, C. E. M., Nov 2023, In: Journal of inherited metabolic disease. 46, 6, p. 1017-1028 12 p.Research output: Contribution to journal › Article › Academic › peer-review
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Development of medicines for rare diseases and inborn errors of metabolism: Toward novel public–private partnerships
Rosenberg, N., Stolwijk, N. N., van den Berg, S., Heus, J. J., van der Wel, V., van Gelder, T., Bosch, A. M., de Visser, S. J. & Hollak, C. E. M., Sept 2023, In: Journal of inherited metabolic disease. 46, 5, p. 806-816 11 p.Research output: Contribution to journal › Review article › Academic › peer-review
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