Amsterdam Gastroenterology Endocrinology Metabolism
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Medicine Development and Access for Rare Diseases: Can We Do Better?
Hollak, C. E. M., Rosenberg, N., Post, C., Stolwijk, N., Manders, E., Schoenmakers, D., Penninx, B., Reijnhout, N., Verdeyen, K., Jonker, R., Bosch, A. M., Langeveld, M., van der Wel, V., de Visser, S. & van den Berg, S., Mar 2026, In: Journal of inherited metabolic disease. 49, 2, p. e70146 e70146.Research output: Contribution to journal › Review article › Academic › peer-review
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Access to anticancer and orphan medicines through compassionate use programs and named patient basis in seven European countries
Rosenberg, N., Post, H. C., Schutte, T., de Visser, S. J., Bartelink, I., Pasmooij, A. M. G., van Laarhoven, H. W. M. & Hollak, C. E. M., 1 Nov 2025, In: ESMO open. 10, 11, 105855.Research output: Contribution to journal › Article › Academic › peer-review
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Application of four pricing models for orphan medicines: a case study for lumasiran
Rosenberg, N., Manders, E., van den Berg, S., Deesker, L. J., Garrelfs, S. F., de Visser, S. J., Groothoff, J. W. & Hollak, C. E. M., 1 Dec 2024, In: Orphanet Journal of Rare Diseases. 19, 1, 485.Research output: Contribution to journal › Article › Academic › peer-review
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